KCNT1 inhibitors and methods of use
Grant
US12583849B2
Kind: B2
Mar 24, 2026
Assignee
PRAXIS PRECISION MEDICINES, INC.
Inventors
Andrew Mark Griffin, Gabriel Martinez Botella, Brian Edward Marron, Paul S. Charifson
Abstract
The present invention is directed to, in part, compounds and compositions useful for preventing and/or treating a neurological disease or disorder, a disease or condition relating to excessive neuronal excitability, and/or a gain-of-function mutation in a gene (e.g., KCNT1). Methods of treating a neurological disease or disorder, a disease or condition relating to excessive neuronal excitability, and/or a gain-of-function mutation in a gene such as KCNT1 are also provided herein.
CPC Classifications
C07D 417/12
C07D 413/14
C07D 413/04
C07D 471/04
Filing Date
2021-02-26
Application No.
17904963
Claims
14