Method and drug for treating spinal muscular atrophy
Grant
US12576139B2
Kind: B2
Mar 17, 2026
Assignee
Talengen International Limited
Inventors
Jinan Li
Abstract
Provided is a method for treating spinal muscular atrophy (SMA), comprising: administrating a therapeutically effective amount of a plasminogen pathway activator to a subject. Further provided are a pharmaceutical composition, product and kit comprising said plasminogen pathway activator, which are used for treating spinal muscular atrophy.
CPC Classifications
A61K 38/48
A61K 9/0019
A61K 9/0073
A61K 38/484
A61K 38/49
A61P 11/00
A61P 21/00
A61P 25/00
A61P 29/00
C12Y 304/21007
Filing Date
2020-11-17
Application No.
17924617
Claims
13