COMPOSITIONS FOR USE IN THE TREATMENT OF CHD2 HAPLOINSUFFICIENCY
Application
US20260085319A1
Kind: A1
Mar 26, 2026
Inventors
Igor ULITSKY, Caroline Jane ROSS
Abstract
A method of increasing an amount of Chromodomain Helicase DNA Binding Protein 2 (CHD2) in a neuronal cell is provided. The method comprising introducing into the cell a nucleic acid agent directed at the last exon of human Chaserr, thereby increasing the amount of CHD2 in the neuronal cell.
CPC Classifications
C12N 15/1137
A61P 25/00
G16B 30/10
C12N 2310/11
C12N 2310/321
Filing Date
2025-08-26
Application No.
19310181