METHODS OF TREATING FABRY DISEASE IN PATIENTS HAVING RENAL IMPAIRMENT
Application
US20260076951A1
Kind: A1
Mar 19, 2026
Assignee
Amicus Therapeutics, Inc.
Inventors
Franklin Johnson
Abstract
Provided are methods of treating Fabry disease in a patient having severe renal impairment. A method for the treatment of Fabry disease in a patient having severe renal impairment, including administering to the patient about 50 mg to about 200 mg free base equivalent (FBE) of migalastat or salt thereof at a frequency of less than once every week. A method for the treatment of Fabry disease in a patient having severe renal impairment, including administering to the patient about 50 mg to about 100 mg free base equivalent of migalastat or salt thereof at a frequency of between about once every three days and about once every two weeks.
CPC Classifications
A61K 31/445
A61P 13/12
Filing Date
2025-09-19
Application No.
19333835