RNAI TARGETING KIF1A MISSENSE MUTATIONS FOR TREATMENT OF KIF1A ASSOCIATED NEUROLOGICAL DISORDER
Publication
EP4709862A2
Kind: A2
Mar 18, 2026
Applicants
Ovid Therapeutics Inc.
Inventors
GERMAIN, Noelle
IPC Classifications
C12N 15/113 20100101AFI20251212BHEP
A61K 31/7105 20060101ALI20251212BHEP
A61K 48/00 20060101ALI20251212BHEP
Designated States
AL, AT, BE, BG, CH, CY, CZ, DE, DK, EE, ES, FI, FR, GB, GR, HR, HU, IE, IS, IT, LI, LT, LU, LV, MC, ME, MK, MT, NL, NO, PL, PT, RO, RS, SE, SI, SK, SM, TR