THERAPEUTIC CRISPR/CAS9 GENE EDITING APPROACHES TO THE C9ORF72 REPEAT EXPANSION MUTATION IN IPSCS
Publication
EP4709861A2
Kind: A2
Mar 18, 2026
Applicants
THE REGENTS OF THE UNIVERSITY OF CALIFORNIA
Inventors
CLELLAND, Claire
IPC Classifications
C12N 15/113 20100101AFI20251212BHEP
C12N 9/22 20060101ALI20251212BHEP
A61K 31/7105 20060101ALI20251212BHEP
A61K 48/00 20060101ALI20251212BHEP
C12N 15/10 20060101ALI20251212BHEP
C12N 15/864 20060101ALI20251212BHEP
A61P 25/28 20060101ALI20251212BHEP
Designated States
AL, AT, BE, BG, CH, CY, CZ, DE, DK, EE, ES, FI, FR, GB, GR, HR, HU, IE, IS, IT, LI, LT, LU, LV, MC, ME, MK, MT, NL, NO, PL, PT, RO, RS, SE, SI, SK, SM, TR