TARGETED TREATMENT OF SPLICEOPATHY-INDUCED NEUROLOGICAL DISORDERS
Publication
EP4630558A2
Kind: A2
Mar 18, 2026
Applicants
Auttx, LLC
Inventors
DRAPER, Isabelle, KOPIN, Alan S., BROWN, Duncan
IPC Classifications
C12N 15/113 20100101AFI20250625BHEP
A61K 31/7115 20060101ALI20250625BHEP
Designated States
AL, AT, BE, BG, CH, CY, CZ, DE, DK, EE, ES, FI, FR, GB, GR, HR, HU, IE, IS, IT, LI, LT, LU, LV, MC, ME, MK, MT, NL, NO, PL, PT, RO, RS, SE, SI, SK, SM, TR