ASSAYS FOR DIAGNOSING AND EVALUATING TREATMENT OPTIONS FOR FABRY DISEASE
Publication
EP4541418A2
Kind: A2
Mar 18, 2026
Applicants
Amicus Therapeutics, Inc., NATIONAL INSTITUTES OF HEALTH
Inventors
Lockhart, David, Castelli, Jeff
IPC Classifications
G01N 33/53 20060101AFI20250605BHEP
G01N 33/567 20060101ALI20250605BHEP
G01N 33/573 20060101ALI20250605BHEP
A61K 31/435 20060101ALI20250605BHEP
A61K 31/445 20060101ALI20250605BHEP
A61K 31/45 20060101ALI20250605BHEP
A61P 3/00 20060101ALI20250605BHEP
A61P 9/10 20060101ALI20250605BHEP
A61P 43/00 20060101ALI20250605BHEP
A61P 13/12 20060101ALI20250605BHEP
C07D 211/46 20060101ALI20250605BHEP
G01N 33/50 20060101ALI20250605BHEP
A61K 45/06 20060101ALI20250605BHEP
A61P 9/00 20060101ALI20250605BHEP
Designated States
AT, BE, BG, CH, CY, CZ, DE, DK, EE, ES, FI, FR, GB, GR, HU, IE, IS, IT, LI, LT, LU, LV, MC, MT, NL, PL, PT, RO, SE, SI, SK, TR