COMPOUNDS AND METHODS USEFUL FOR STABILIZING PHENYLALANINE HYDROXYLASE MUTATIONS
Publication
EP4486749A1
Kind: A1
Mar 18, 2026
Applicants
Agios Pharmaceuticals, Inc.
Inventors
DE PASCALIS, Lucrezia, FINLAY, Heather Jane, KING, Sandra, KONTEATIS, Zenon D., SHOOK, Brian C.
IPC Classifications
C07D 519/00 20060101AFI20230901BHEP
A61P 25/00 20060101ALI20230901BHEP
A61K 31/437 20060101ALI20230901BHEP
Designated States
AL, AT, BE, BG, CH, CY, CZ, DE, DK, EE, ES, FI, FR, GB, GR, HR, HU, IE, IS, IT, LI, LT, LU, LV, MC, ME, MK, MT, NL, NO, PL, PT, RO, RS, SE, SI, SK, SM, TR