(4-BENZO[D]OXAZOL-2-YL)-6,7-DIHYDRO-1H-IMIDAZO[4,5-C]PYRIDINE-5(4H)-YL)METHANONE DERIVATIVES AS MUTANT PAH STABILIZERS FOR THE TREATMENT OF PHENYLKETONURIA
Publication
EP4486744A1
Kind: A1
Mar 18, 2026
Applicants
Agios Pharmaceuticals, Inc.
Inventors
DE PASCALIS, Lucrezia, KING, Sandra, KONTEATIS, Zenon D., SHOOK, Brian C.
IPC Classifications
C07D 471/04 20060101AFI20230901BHEP
C07D 487/04 20060101ALI20230901BHEP
C07D 519/00 20060101ALI20230901BHEP
A61K 31/437 20060101ALI20230901BHEP
A61P 25/00 20060101ALI20230901BHEP
Designated States
AL, AT, BE, BG, CH, CY, CZ, DE, DK, EE, ES, FI, FR, GB, GR, HR, HU, IE, IS, IT, LI, LT, LU, LV, MC, ME, MK, MT, NL, NO, PL, PT, RO, RS, SE, SI, SK, SM, TR