COMPOUNDS AND METHODS USEFUL FOR STABILIZING PHENYLALANINE HYDROXYLASE MUTATIONS
Publication
EP4486447A1
Kind: A1
Mar 18, 2026
Applicants
Agios Pharmaceuticals, Inc.
Inventors
KING, Sandra, KONTEATIS, Zenon, D., SHOOK, Brian, C.
IPC Classifications
A61P 25/00 20060101AFI20230901BHEP
C07D 471/04 20060101ALI20230901BHEP
C07D 487/04 20060101ALI20230901BHEP
C07D 519/00 20060101ALI20230901BHEP
A61K 31/437 20060101ALI20230901BHEP
Designated States
AL, AT, BE, BG, CH, CY, CZ, DE, DK, EE, ES, FI, FR, GB, GR, HR, HU, IE, IS, IT, LI, LT, LU, LV, MC, ME, MK, MT, NL, NO, PL, PT, RO, RS, SE, SI, SK, SM, TR