← EPO Patent Bulletin

METHODS FOR TREATMENT OF ORNITHINE TRANSCARBAMYLASE (OTC) DEFICIENCY

Publication EP4466367A1 Kind: A1 Mar 18, 2026

Applicants

The Trustees of The University of Pennsylvania

Inventors

WANG, Lili, WILSON, James, M., TRETIAKOVA, Anna

IPC Classifications

C12N 15/86 20060101AFI20260210BHEP C07K 14/075 20060101ALI20260210BHEP C12N 9/10 20060101ALI20260210BHEP

Designated States

AL, AT, BE, BG, CH, CY, CZ, DE, DK, EE, ES, FI, FR, GB, GR, HR, HU, IE, IS, IT, LI, LT, LU, LV, MC, ME, MK, MT, NL, NO, PL, PT, RO, RS, SE, SI, SK, SM, TR