SNRNA TARGETING USH2A PRE-MRNA AND APPLICATION THEREOF
Publication
EP4461306A1
Kind: A1
Mar 18, 2026
Applicants
Guangzhou Reforgene Medicine Co., Ltd.
Inventors
LIANG, Junbin, OU, Jiayu, XU, Hui, LIN, Simiao
IPC Classifications
C12N 15/113 20100101AFI20260211BHEP
A61K 38/46 20060101ALI20260211BHEP
A61K 47/26 20060101ALI20260211BHEP
C12N 7/00 20060101ALI20260211BHEP
C12N 9/22 20060101ALI20260211BHEP
Designated States
AL, AT, BE, BG, CH, CY, CZ, DE, DK, EE, ES, FI, FR, GB, GR, HR, HU, IE, IS, IT, LI, LT, LU, LV, MC, ME, MK, MT, NL, NO, PL, PT, RO, RS, SE, SI, SK, SM, TR