GENE THERAPY FOR LAMIN A - ASSOCIATED DEFICIENCIES
Publication
EP4453226A1
Kind: A1
Mar 18, 2026
Applicants
The Trustees of the University of Pennsylvania
Inventors
HINDERER, Christian
IPC Classifications
C12N 15/86 20060101AFI20260210BHEP
A61P 9/00 20060101ALI20260210BHEP
A61K 48/00 20060101ALI20260210BHEP
A61P 21/00 20060101ALI20260210BHEP
A61K 38/00 20060101ALI20260210BHEP
Designated States
AL, AT, BE, BG, CH, CY, CZ, DE, DK, EE, ES, FI, FR, GB, GR, HR, HU, IE, IS, IT, LI, LT, LU, LV, MC, ME, MK, MT, NL, NO, PL, PT, RO, RS, SE, SI, SK, SM, TR