METHODS OF TREATING MYOTONIC DYSTROPHY TYPE 1 USING PEPTIDE-OLIGONUCLEOTIDE CONJUGATES
Publication
EP4304657A2
Kind: A2
Apr 01, 2026
Applicants
Pepgen Inc.
Inventors
GODFREY, Caroline, BRACEGIRDLE, Sonia, HOLLAND, Ashling, GUNNOO, Smita
IPC Classifications
A61K 47/64 20170101AFI20230929BHEP
A61P 21/04 20060101ALI20230929BHEP
C07K 9/00 20060101ALI20230929BHEP
C12N 15/113 20100101ALI20230929BHEP
C12Q 1/68 20180101ALI20230929BHEP
A61P 25/28 20060101ALI20230929BHEP
Designated States
AL, AT, BE, BG, CH, CY, CZ, DE, DK, EE, ES, FI, FR, GB, GR, HR, HU, IE, IS, IT, LI, LT, LU, LV, MC, MK, MT, NL, NO, PL, PT, RO, RS, SE, SI, SK, SM, TR