HUMAN CHROMOSOME 9 OPEN READING FRAME 72 (C9ORF72) IRNA AGENT COMPOSITIONS AND METHODS OF USE THEREOF
Publication
EP4073251A1
Kind: A1
Mar 25, 2026
Applicants
Alnylam Pharmaceuticals, Inc., Regeneron Pharmaceuticals, Inc.
Inventors
FISHILEVICH, Elane, MILSTEIN, Stuart, BROWN, Kirk, ZIMMERMANN, Tracy, MCININCH, James, D., FRENDEWEY, David, CHIAO, Eric, SHARMA-KANNING, Aarti, GAGLIARDI, Anthony, DROGUETT, Gustavo, DUBOSE, Brittany, ZAMBROWICZ, Brian
IPC Classifications
C12N 15/113 20100101AFI20260217BHEP
A61K 31/713 20060101ALI20260217BHEP
A61P 25/28 20060101ALI20260217BHEP
Designated States
AL, AT, BE, BG, CH, CY, CZ, DE, DK, EE, ES, FI, FR, GB, GR, HR, HU, IE, IS, IT, LI, LT, LU, LV, MC, MK, MT, NL, NO, PL, PT, RO, RS, SE, SI, SK, SM, TR