COUPLING ENDONUCLEASES WITH END-PROCESSING ENZYMES DRIVES HIGH EFFICIENCY GENE DISRUPTION
Publication
EP4062927A1
Kind: A1
Mar 18, 2026
Applicants
Seattle Children's Research Institute
Inventors
SCHARENBERG, Andrew, M., CERTO, Michael, T., GWIAZDA, Kamila, Sabina
IPC Classifications
A61K 38/46 20060101AFI20220811BHEP
A61K 38/45 20060101ALI20220811BHEP
A61K 38/52 20060101ALI20220811BHEP
C12N 9/12 20060101ALI20220811BHEP
C12N 9/22 20060101ALI20220811BHEP
C12N 9/90 20060101ALI20220811BHEP
C12N 15/62 20060101ALI20220811BHEP
A61P 31/18 20060101ALI20220811BHEP
A61P 37/02 20060101ALI20220811BHEP
C12N 15/10 20060101ALI20220811BHEP
Designated States
AL, AT, BE, BG, CH, CY, CZ, DE, DK, EE, ES, FI, FR, GB, GR, HR, HU, IE, IS, IT, LI, LT, LU, LV, MC, MK, MT, NL, NO, PL, PT, RO, RS, SE, SI, SK, SM, TR