OLIGONUCLEOTIDES FOR MODULATING ATXN2 EXPRESSION
Publication
EP3947677A1
Kind: A1
Mar 18, 2026
Applicants
F. Hoffmann-La Roche AG
Inventors
HAGEDORN, Peter, HANSEN, Dennis Jul, HUDLEBUSCH, Heidi Rye, LADEFOGED, Mette, PEDERSEN, Lykke, RASMUSSEN, Soren V
IPC Classifications
C12N 15/113 20100101AFI20201009BHEP
A61K 31/7115 20060101ALI20201009BHEP
A61K 31/712 20060101ALI20201009BHEP
A61K 31/7125 20060101ALI20201009BHEP
A61P 25/00 20060101ALI20201009BHEP
Designated States
AL, AT, BE, BG, CH, CY, CZ, DE, DK, EE, ES, FI, FR, GB, GR, HR, HU, IE, IS, IT, LI, LT, LU, LV, MC, MK, MT, NL, NO, PL, PT, RO, RS, SE, SI, SK, SM, TR