COMPOSITIONS AND METHODS COMPRISING A TTR GUIDE RNA AND A POLYNUCLEOTIDE ENCODING AN RNA-GUIDED DNA BINDING AGENT
Publication
EP3946598A1
Kind: A1
Apr 01, 2026
Applicants
Intellia Therapeutics, Inc.
Inventors
CHANG, Yong, ALEXANDER, Seth C., WOOD, Kristy M., KANJOLIA, Arti Mahendra Prakash, ODATE, Shobu, SEITZER, Jessica Lynn, LESCARBEAU, Reynald Michael, STRAPPS, Walter
IPC Classifications
A61P 25/00 20060101AFI20201002BHEP
A61K 31/713 20060101ALI20201002BHEP
A61P 25/28 20060101ALI20201002BHEP
C12N 9/22 20060101ALI20201002BHEP
C12N 15/113 20100101ALI20201002BHEP
Designated States
AL, AT, BE, BG, CH, CY, CZ, DE, DK, EE, ES, FI, FR, GB, GR, HR, HU, IE, IS, IT, LI, LT, LU, LV, MC, MK, MT, NL, NO, PL, PT, RO, RS, SE, SI, SK, SM, TR