COMPOSITIONS AND METHODS FOR TREATING OCULOPHARYNGEAL MUSCULAR DYSTROPHY (OPMD)
Publication
EP3931317A1
Kind: A1
Mar 25, 2026
Applicants
Benitec IP Holdings Inc.
Inventors
STRINGS-UFOMBAH, Vanessa, SUHY, David, KAO, Shih-Chu, ROELVINK, Petrus W.
IPC Classifications
C12N 15/86 20060101AFI20221201BHEP
C12N 15/113 20100101ALI20221201BHEP
A61K 48/00 20060101ALI20221201BHEP
C07K 14/47 20060101ALI20221201BHEP
C07K 14/005 20060101ALI20221201BHEP
Designated States
AL, AT, BE, BG, CH, CY, CZ, DE, DK, EE, ES, FI, FR, GB, GR, HR, HU, IE, IS, IT, LI, LT, LU, LV, MC, MK, MT, NL, NO, PL, PT, RO, RS, SE, SI, SK, SM, TR