CRISPR/CAS-RELATED METHODS AND COMPOSITIONS FOR TREATING DUCHENNE MUSCULAR DYSTROPHY AND BECKER MUSCULAR DYSTROPHY
Publication
EP3748004A1
Kind: A1
Mar 18, 2026
Applicants
Editas Medicine, Inc.
Inventors
HSU, Patrick, David, MAEDER, Morgan, Lee, ODONNELL, Penrose, TYCKO, Joshua, C., HUSTON, Nicholas, C.
IPC Classifications
C12N 15/113 20100101AFI20201015BHEP
C12N 15/10 20060101ALI20201015BHEP
C12N 9/22 20060101ALI20201015BHEP
C12N 9/52 20060101ALI20201015BHEP
Designated States
AL, AT, BE, BG, CH, CY, CZ, DE, DK, EE, ES, FI, FR, GB, GR, HR, HU, IE, IS, IT, LI, LT, LU, LV, MC, MK, MT, NL, NO, PL, PT, RO, RS, SE, SI, SK, SM, TR