POLYNUCLEOTIDES ENCODING ORNITHINE TRANSCARBAMYLASE FOR THE TREATMENT OF UREA CYCLE DISORDERS
Grant
EP3714048B1
Kind: B1
Mar 18, 2026
Inventors
ZHUO, Zhijian, FRASSETTO, Andrea Lea, MARTINI, Paolo G.V., FINN, Patrick, PRESNYAK, Vladimir
IPC Classifications
C12N 9/10 20060101AFI20190531BHEP
C12N 15/67 20060101ALI20190531BHEP
A61K 48/00 20060101ALI20190531BHEP
A61P 3/00 20060101ALI20190531BHEP
Designated States
AL, AT, BE, BG, CH, CY, CZ, DE, DK, EE, ES, FI, FR, GB, GR, HR, HU, IE, IS, IT, LI, LT, LU, LV, MC, MK, MT, NL, NO, PL, PT, RO, RS, SE, SI, SK, SM, TR