COMPOSITIONS AND METHODS FOR TTR GENE EDITING AND TREATING ATTR AMYLOIDOSIS
Publication
EP3688161A1
Kind: A1
Apr 01, 2026
Applicants
Intellia Therapeutics, Inc.
Inventors
KANJOLIA, Arti Mahendra Prakash, ODATE, Shobu, SEITZER, Jessica Lynn, LESCARBEAU, Reynald Michael, STRAPPS, Walter
IPC Classifications
C12N 15/113 20100101AFI20210409BHEP
C12N 15/10 20060101ALI20210409BHEP
A61K 48/00 20060101ALI20210409BHEP
A61P 25/28 20060101ALI20210409BHEP
Designated States
AL, AT, BE, BG, CH, CY, CZ, DE, DK, EE, ES, FI, FR, GB, GR, HR, HU, IE, IS, IT, LI, LT, LU, LV, MC, MK, MT, NL, NO, PL, PT, RO, RS, SE, SI, SK, SM, TR