ENZYMATIC REPLACEMENT THERAPY AND ANTISENSE THERAPY FOR POMPE DISEASE
Publication
EP3638788A1
Kind: A1
Mar 18, 2026
Applicants
Erasmus University Medical Center Rotterdam
Inventors
VAN DER WAL, Erik, BERGSMA, Atze Jacobus, PIJNAPPEL, Wilhelmus Wenceslaus Matthias, VAN DER PLOEG, Antje Tjitske
IPC Classifications
C12N 15/113 20100101AFI20181221BHEP
A61K 31/712 20060101ALI20181221BHEP
A61K 31/7125 20060101ALI20181221BHEP
A61K 48/00 20060101ALI20181221BHEP
Designated States
AL, AT, BE, BG, CH, CY, CZ, DE, DK, EE, ES, FI, FR, GB, GR, HR, HU, IE, IS, IT, LI, LT, LU, LV, MC, MK, MT, NL, NO, PL, PT, RO, RS, SE, SI, SK, SM, TR