ANTISENSE TARGETING DYNAMIN 2 AND USE FOR THE TREATMENT OF CENTRONUCLEAR MYOPATHIES AND NEUROPATHIES
Publication
EP3610016A1
Kind: A1
Mar 18, 2026
Applicants
Genethon, Institut National de la Santé et de la Recherche Médicale, Universite d'Evry Val d'Essonne
Inventors
BUJ BELLO, Ana Maria
IPC Classifications
C12N 15/113 20100101AFI20181019BHEP
A61K 31/712 20060101ALI20181019BHEP
C07H 21/02 20060101ALI20181019BHEP
A61P 21/00 20060101ALI20181019BHEP
Designated States
AL, AT, BE, BG, CH, CY, CZ, DE, DK, EE, ES, FI, FR, GB, GR, HR, HU, IE, IS, IT, LI, LT, LU, LV, MC, MK, MT, NL, NO, PL, PT, RO, RS, SE, SI, SK, SM, TR