POLYNUCLEOTIDES ENCODING CITRIN FOR THE TREATMENT OF CITRULLINEMIA TYPE 2
Publication
EP3458081A1
Kind: A1
Mar 18, 2026
Applicants
ModernaTX, Inc.
Inventors
MARTINI, Paolo, HOGE, Stephen, BENENATO, Kerry, PRESNYAK, Vladimir, MCFADYEN, Iain, KUMARASINGHE, Ellalahewage Sathyajith, CAO, Jinsong, GUEY, Lin Tung, SABNIS, Staci
IPC Classifications
A61K 31/7088 20060101AFI20250919BHEP
C07K 14/47 20060101ALI20250919BHEP
A61P 3/00 20060101ALI20250919BHEP
A61P 13/00 20060101ALI20250919BHEP
A61K 9/51 20060101ALI20250919BHEP
A61K 38/00 20060101ALI20250919BHEP
Designated States
AL, AT, BE, BG, CH, CY, CZ, DE, DK, EE, ES, FI, FR, GB, GR, HR, HU, IE, IS, IT, LI, LT, LU, LV, MC, MK, MT, NL, NO, PL, PT, RO, RS, SE, SI, SK, SM, TR