METHODS AND COMPOSITIONS FOR INHIBITING PMP22 EXPRESSION
Publication
EP3426349A1
Kind: A1
Apr 01, 2026
Applicants
Ionis Pharmaceuticals, Inc.
Inventors
HUNG, Gene, KORDASIEWICZ, Holly, ZHAO, Hien, Thuy, SWAYZE, Eric, E.
IPC Classifications
C12N 15/113 20100101AFI20191122BHEP
A61K 31/7088 20060101ALI20191122BHEP
A61P 25/00 20060101ALI20191122BHEP
A61P 25/02 20060101ALI20191122BHEP
A61P 25/28 20060101ALI20191122BHEP
Designated States
AL, AT, BE, BG, CH, CY, CZ, DE, DK, EE, ES, FI, FR, GB, GR, HR, HU, IE, IS, IT, LI, LT, LU, LV, MC, MK, MT, NL, NO, PL, PT, RO, RS, SE, SI, SK, SM, TR